Tag Archives: Johns Hopkins Medicine

Johns Hopkins researchers identify new biological target for treating spinal muscular atrophy

lncRNA

Johns Hopkins researchers along with academic and drug industry investigators say they have identified a new biological target for treating spinal muscular atrophy. They report they have evidence that an experimental medicine aimed at this target works as a “booster” in conjunction with a drug called nusinersen that was recently FDA-approved to improve symptoms of the disorder in mice. In ...

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